US lawmakers take FDA to task over rare diseases record
Lawmakers and patient advocates in the US are concerned that the FDA's regulation of rare disease therapies has been inconsistent and overly cautious.
Newsletters and Deep Dive digital magazine
Lawmakers and patient advocates in the US are concerned that the FDA's regulation of rare disease therapies has been inconsistent and overly cautious.
Innovative trial designs that harness data augmentation, RWD, and the power of AI are enabling a new era of rare disease research.
AI-powered drug developer Generate Biomedicine completes a $400m IPO, the largest for biotech on the Nasdaq so far this year.
The future of clinical trials isn’t about replacing people. It’s about empowering them with smarter tools.
Boehringer Ingelheim's partnership with Sitryx is focused on a family of small-molecule drugs for autoimmune and inflammatory diseases.
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