
PTC’s gene therapy for rare disease cleared for NHS use
Upstaza has shown impressive clinical results in children with fatal disorder AADC deficiency.
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Upstaza has shown impressive clinical results in children with fatal disorder AADC deficiency.
Drug is first new echinocandin to be approved for marketing in the US in more than a decade.
But unanimous vote on biomarker validity could support accelerated approval of tofersen.
APACMed and Eversana join forces to draw up coverage frameworks applicable to APAC countries.
Delay could narrow the gap between AbbVie's product and a rival system from Mitsubishi Tanabe.
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