X
FDA gives go-ahead for CRISPR-based sickle cell disease trial
https://pharmaphorum.com/news/fda-gives-go-ahead-for-crispr-based-sickle-cell-disease-trial/
Vertex
Digital health round-up: Vertex’s machine learning tie-up and more
US pharma hopes to tap into potential of machine learning
Vertex and Genomics collaborate to discover new drug targets
Project will use machine learning and algorithms to find new targets
Vertex’s Orkambi CF drug okayed for funding in Australia
Committee recommends outcomes-based deal
US regulators expand label for Vertex’s Kalydeco CF drug
New label includes children aged 12-24 months
CF patients furious as Vertex turns back on NICE
Patients in England could be denied access to drug
