News Amicus to file Fabry drug after FDA changes mind Regulator drops demand for further phase 3 trial.
News Sarepta announces Allergan veteran as next CEO Sarepta has announced former Allergan president Doug Ingram will be its new CEO.
News More good news for Bluebird Bio with CALD gene therapy Bluebird Bio has presented encouraging data from its gene therapy treatment for t
News UK patients gain early access to Duchenne drug Patients to get Santhera's Raxone under EAMS scheme.
News UK's Mission divests kidney drug to Dimerix for $292m Mission Therapeutics has struck a deal to out-license a drug for acute kidney injury to Australia's Dimerix, sharpening its focus on CNS diseases.
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