News Charities unite to oppose NICE rare disease rules MPs to discuss controversial plan in special debate.
News FDA fast tracks Shire clotting disease drug The US regulator has given a Fast Track designation to a Shire pipeline drug for a life-threatening blood clotting disease, hereditary thrombotic thrombocytopenic purpura.
Views & Analysis Horses or zebras: inspiring behavioural change to make the r... Insight into human behaviour allows development of programmes that help doctors diagnose rare diseases.
News Thanks Mr President, but you’re wrong about FDA, says rare d... NORD patient advocacy group responds to Congress speech
News Teva files orphan blockbuster hope in tardive dyskinesia SD-809 will be vital for Teva if approved.
Sales & Marketing Biotech is back, with Craig Ackerman In Philadelphia this month, pharmaphorum spoke with Craig Ackerman, a partner at the Alexander Group, about launches, AI best practices, and more.
Sales & Marketing Sponsored Using AI-driven synthetic personas to take your insights fur... As AI continues to reshape the healthcare landscape, pharma teams are beginning to leverage synthetic personas.