News US regulator grants $23 million to rare disease R&D FDA announces 21 rare disease clinical trial research grants.
News US and EU regulators collaborate on rare diseases Clinical trial design among areas regulators will collaborate on
News Biomarker trial to show drug value in rare lung disease Growing incidence of IPF raises need for better means of determining diagnosis and treatment success.
News Vertex hit by phase 3 cystic fibrosis failure Company looks to other CF sub-groups to yield success
Views & Analysis Meeting the challenges of rare disease treatment adherence HCPs, pharma and patients can pool their experience to develop effective, tailored support.
R&D The long-delayed promise of the microbiome, with Sam Possemi... Sam Possemiers, CEO of MRM Health, believes that the microbiome space is finally coming into maturity.
Sales & Marketing Sponsored How to meet your physicians where they are online A pharma company’s core mission is to improve patient outcomes. This hinges on effectively influencing HCP clinical behaviour and driving disease education.
