Rare Disease Day

R&D

Rare Disease R&D: one step forward, but a long road ahead

With over 40% of all medicines in the pipeline aimed at rare diseases, the future looks positive for increasing the number of treatments available.

News

Rare diseases have tenfold higher impact on healthcare costs...

A new study has suggested that the economic burden posed by rare diseases is around 10 times higher than for common "mass market" conditions.

Views & Analysis

Why research into the mental health impact of a rare disease diagnosis is long overdue

Why we need research into the mental health impact of a rare...

Rare diseases impact between 3.5%-5.9% of the world’s population.

Views & Analysis

Expediting Innovations in Rare Disease Domain

Expediting innovation in the rare disease domain

Rare diseases affect a fraction of the population – 450 million+ peop

Views & Analysis

Rare disease insights from the patient community

To help pharma companies understand what life is really like for patients with a rare disease, a new resource has been released to coincide with Rare Disease Day 2021.

Views & Analysis

Building a better future for people with rare diseases in al...

How has rare disease care changed over the last few years? And what might we expect from the next five?

Rare Disease R&D: one step forward, but a long road ahead

Rare diseases have tenfold higher impact on healthcare costs...

Why we need research into the mental health impact of a rare...

Expediting innovation in the rare disease domain

Rare disease insights from the patient community

Building a better future for people with rare diseases in al...

Biotech is back, with Craig Ackerman

Using AI-driven synthetic personas to take your insights fur...

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