neurodegenerative disease

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PTC slides on failed Friedreich ataxia study

PTC Therapeutics has cued up no fewer than three clinical trial readouts this quarter that could lead to new regulatory filings – but the latest for vatiquinone in inherit

News

Patients dismayed as FDA advisors narrowly reject Amylyx' AL...

By a narrow margin, an FDA advisory committee has voted against approval of Amylyx' experimental medicine for amyotrophic lateral sclerosis until the company can provide more evidence that

News

After ph2 win, Cerevance preps pivotal trials of novel Parki...

Cerevance has said it plans to move on to late-stage trials of its first-in-class Parkinson's disease drug CVN424 after hitting the mark in a phase 2 proof-of-concept study.

News

Amylyx slumps on non-committal FDA reviewer assessment of AL...

Shares in Amylyx Pharma slid today after the FDA published a less-than-enthusiastic assessment of its amyotrophic lateral sclerosis (ALS) therapy ahead of an advisory committee meeting on W

News

Blow to Biogen as ALS hope tofersen flunks phase 3 trial

Already struggling to make headway with its recently launched Alzheimer's drug, Biogen suffered a major late-stage pipeline setback after its tofersen drug for amyotrophic lateral sclerosis

News

Bad news for Biohaven as verdiperstat flunks first phase 3 t...

Biohaven's key pipeline drug verdiperstat has failed to have any Therapeutic effect in patients with the rare neurological disorder multiple system atrophy (MSA) – its lead indication – but

PTC slides on failed Friedreich ataxia study

Patients dismayed as FDA advisors narrowly reject Amylyx' AL...

After ph2 win, Cerevance preps pivotal trials of novel Parki...

Amylyx slumps on non-committal FDA reviewer assessment of AL...

Blow to Biogen as ALS hope tofersen flunks phase 3 trial

Bad news for Biohaven as verdiperstat flunks first phase 3 t...

Health Innovators – Jennifer Schranz

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