News FDA approves Roche potential haemophilia blockbuster Blood cancer drug Gazyva also gets new US use
News A gamechanger in haemophilia? SOBI unruffled by Roche's impe... The received wisdom is that a generation of new products in haemophilia A, led by Roche’s emicizumab and potentially curative gene therapies, will bring about a transformation of treatment
News Breakthrough status for BioMarin ratchets up haemophilia A c... The FDA has granted Breakthrough Therapy Designation to BioMarin’s gene therapy for haemophilia A, helping to intensify competition in the field.
News Alnylam halts trials of haemophilia drug after patient death Trials will resume once safety protocols have been reviewed.
News FDA grants fast review for Roche's haemophilia drug Emicizumab is firm's latest blockbuster hopeful
News Shire injunction blocks Roche's 'misleading' statements on h... Shire alleges trial info "unlawfully disparages" its product.
News Neurogene drops high-dose arm in Rett study after death The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died
Sales & Marketing Coming soon: The Life Sciences Industry Report 2025 – insigh... Prepare for 2025 with pharmaphorum’s Life Sciences Report, featuring expert insights on AI in drug development, gene therapy, and top industry trends
