gene therapy

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Novartis puts up $1.7bn for Voyager's gene therapy platform

Voyager Therapeutics has signed another big pharma partner for its TRACER adeno-associated virus (AAV) vector technology, designed to improve the safety of gene therapies, with Novartis tak

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bluebird says future uncertain as delays to gene therapies b...

As bluebird bio struggles to get its gene therapies over the finishing line, the company says its financial position raises "substantial doubt" about its ability to continue as a going conc

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2nd Annual Gene Therapy Patient Engagement Summit

Integrate the Patient Voice

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Takeda grows in gene therapies again with $2bn Code Bio deal

Takeda has forged another alliance as it continues a push into gene therapy, agreeing a deal worth up to $2 billion with Code Biotherapeutics for opt-in rights to four candidates for rare d

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Regenxbio expands MPS I gene therapy trial after first look ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown

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Astellas says Pompe gene therapy clears safety hurdle

With the safety of gene therapies thrown into the spotlight by a series of FDA clinical holds, Astellas has said that an interim readout in a phase 1/2 trial of its Pompe disease candidate

Novartis puts up $1.7bn for Voyager's gene therapy platform

bluebird says future uncertain as delays to gene therapies b...

2nd Annual Gene Therapy Patient Engagement Summit

Takeda grows in gene therapies again with $2bn Code Bio deal

Regenxbio expands MPS I gene therapy trial after first look ...

Astellas says Pompe gene therapy clears safety hurdle

The long-delayed promise of the microbiome, with Sam Possemi...

How to meet your physicians where they are online

gene therapy

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