gene therapy

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Genetic engineeering concept with 3d rendering robotic hand editing dna helix

PTC gets green light for gene therapy Upstaza in EU

PTC Therapeutic's Upstaza gene therapy for patients with genetic disorder AADC deficiency has been recommended for approval in the EU, setting up another test of the commercial prospects f

News

How-cell-and-gene-therapies-are-transforming-the-pace-of-deal-making

SwanBio raises $56m for rare neurological disease gene thera...

SwanBio Therapeutics has raised $56 million in a second-round financing that will be used to advance its lead gene therapy candidate for adrenomyeloneuropathy (AMN) into clinical testing la

Events

Partner Content

Next Generation RNA Therapeutics Summit

Trailblazing Superior RNA Therapeutics of the Future

News

Astellas takes $170m charge as it drops DMD gene therapies

Astellas has said it will book a $170 million impairment charge in its fourth quarter results as a result of a decision to halt the development of three gene therapy candidates for Duchenne

News

ICER says bluebird bio's $2.1m gene therapy is cost-effectiv...

US cost-effectiveness watchdog ICER has handed bluebird bio some good news ahead of its FDA advisory committee meeting for rare blood disorder gene therapy beti-cel in June, by endorsing it

News

Bluebird sheds a third of its workforce to cut costs

Gene therapy specialist bluebird bio has said 30% of its workforce will lose their jobs, in a bid to conserve cash as it tried to get its lead programmes over the finish line.

PTC gets green light for gene therapy Upstaza in EU

SwanBio raises $56m for rare neurological disease gene thera...

Next Generation RNA Therapeutics Summit

Astellas takes $170m charge as it drops DMD gene therapies

ICER says bluebird bio's $2.1m gene therapy is cost-effectiv...

Bluebird sheds a third of its workforce to cut costs

Court sides with EU on decision to revoke Ocaliva's license

Coming soon: The Life Sciences Industry Report 2025 – insigh...

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