beta thalassaemia

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EMA finds possible link between mRNA COVID jabs and myocardi...

The EU medicines regulator has said that there is some evidence to suggest a possible link between mRNA-based vaccines for COVID-19 and rare cases of heart inflammation.

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EHA21: Study raises BMS' hopes for Reblozyl in less severe d...

Bristol-Myers Squibb has taken another step towards achieving its blockbuster hopes for beta thalassaemia-associated anaemia therapy Reblozyl, after hitting the target in a phase 2 trial in

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engineering and genetic editing through the Crispr technique. DNA chain breaking down. 3D rendering

Zynteglo halt re-ignites viral vector safety concerns; analy...

Bluebird Bio’s decision to hit pause on the launch of Zynteglo for beta thalassaemia after two cases of cancer were seen in a clinical trial could see fears over the safety of viral vectors

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bluebird bio 'baffled' after NICE rejects beta-thalassaemia ...

It’s back to the drawing board for bluebird bio and its discussions with NICE, which has rejected its beta thalassaemia gene therapy Zynteglo for regular NHS use in first draft guidance.

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Bluebird trumpets long-term data from beta-thalassaemia gene...

bluebird bio has presented long-term data from its Zynteglo one-time gene therapy for the blood disorder beta-thalassaemia, as the company continues talks with payers in Europe to bring the

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ASH: CRISPR, Vertex' CTX001 hits the mark in red cell disord...

A gene-editing drug developed by CRISPR Therapeutics and Vertex Pharma has achieved “remarkable” improvements in patients with beta thalassaemia and sickle cell disease in an early-stage tr

EMA finds possible link between mRNA COVID jabs and myocardi...

EHA21: Study raises BMS' hopes for Reblozyl in less severe d...

Zynteglo halt re-ignites viral vector safety concerns; analy...

bluebird bio 'baffled' after NICE rejects beta-thalassaemia ...

Bluebird trumpets long-term data from beta-thalassaemia gene...

ASH: CRISPR, Vertex' CTX001 hits the mark in red cell disord...

Neurogene drops high-dose arm in Rett study after death

Coming soon: The Life Sciences Industry Report 2025 – insigh...

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beta thalassaemia

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