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Saturday 5 July 2025

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News

PTC Therapeutics' chief executive Matthew Klein.

Germany will be first launch for PTC's phenylketonuria drug

PTC Therapeutics' treatment for the rare disease PKU, Sephience, will launch in its first market next month after getting EU approval.

News

Dyvyzat box, bottle, and oral delivery mechanism.

Italfarmaco closes on EU okay for Duchenne drug

Italfarmaco's oral HDAC inhibitor Duvyzat has been recommended for approval in the EU as a treatment for Duchenne muscular dystrophy (DMD).

Editor's Picks

Gilead's twice-yearly PrEP drug is cleared by FDA

Could a Novo error set up early GLP-1 generics in Canada?

23andMe fined £2.31m over UK users' genetic data breach

FDA blocks trials that send US cells to 'hostile' countries

UK regulator overhauls medical device regulation

Oncology

Interview at ASCO 2025 with Dr Danny Nguyen

In pursuit of a cure for cancer: An ASCO 2025 discussion wit...

Dr Danny Nguyen, medical oncologist and haematologist at the City of Hope Orange County, spoke with pharmaphorum at ASCO 2025.

Market Access

pharmaphorum podcast Episode 178a - Sandra Anderson and Chris Williams, Cencora

The value of a partner, globally and locally

A new podcast looks at recent trends related to drug approvals, as well as challenges and opportunities both small and large pharma companies face

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