Views & Analysis Rare Youth Project: Can you empower the next generation of r... The next generation of rare disease advocates need a little support in getting their voices heard as part of the Rare Youth Project.
News EU clears first drug therapy for rare disease cALD Neuraxpharm and Minoryx' Nezglyal has become the first approved drug therapy in the EU for rare neurodegenerative disease cALD.
Digital Sponsored Discover a new era of healthcare panel engagement: Grounded ... A new webinar from Konovo will address some of the critical topics impacting today’s healthcare market research industry.