GM1 gangliosidosis

Views & Analysis

Rare disease families need to stand up and be counted if they want things to change said mum and advocate Christine Waggoner.

News

The FDA stops short of approving leucovorin for autism, but will its clearance for ultra-rare condition CFD-FOLR1 lead to more off-label prescribing?

Sales & Marketing

As AI continues to reshape the healthcare landscape, pharma teams are beginning to leverage synthetic personas.