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News

Vincenzo Nigro, coordinator of the Telethon Undiagnosed Diseases Programme

Italy leads the way on child genetic disease diagnosis

A scheme to hasten the diagnosis of children with genetic disorders is achieving strong results and could be a template for national health systems.

News

FDA clears first gene therapy for rare genetic disease WAS

Fondazione Telethon's Waskyra has become the first gene therapy in the US for Wiskott-Aldrich syndrome, and the first taken to market by a non-profit.

Editor's Picks

CHMP backs Lilly's oral GLP-1 Foundayo for EU approval

RevMed nears EU okay for pancreatic cancer drug Rasonque

Roche adds another obesity drug with $1.16bn Rona deal

MHRA lays out its thinking on AI and medicines regulation

GSK planning 1,200 job cuts in Belgium, says paper

Oncology

pharmaphorum podcast Episode 282 at ESMO26: Dr Chuck Link, Syncromune

ESMO26: Lowering toxicity, extending lives, with Syncromune

As the ESMO26 Congress commences in Madrid, pharmaphorum invited Syncromune Executive Chairman Dr Chuck Link onto the podcast.

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Digital

Discover a new era of healthcare panel engagement: Grounded ...

A new webinar from Konovo will address some of the critical topics impacting today’s healthcare market research industry.

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