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Saturday 15 August 2026

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News

Vincenzo Nigro, coordinator of the Telethon Undiagnosed Diseases Programme

Italy leads the way on child genetic disease diagnosis

A scheme to hasten the diagnosis of children with genetic disorders is achieving strong results and could be a template for national health systems.

News

FDA clears first gene therapy for rare genetic disease WAS

Fondazione Telethon's Waskyra has become the first gene therapy in the US for Wiskott-Aldrich syndrome, and the first taken to market by a non-profit.

Editor's Picks

Trump order upturns federal childhood vaccines policy

Novo Nordisk partners Amazon on London AI hub

England close to eliminating hep C thanks to treatment drive

Lilly, PTC snap up bankrupt Sangamo's main assets

Definium chalks up new phase 3 win for LSD-based therapy

News

Vogenx surpasses expectations with $81M IPO

With $81.3 million raised, Vogenx is the latest in a staggering summer of biotech IPOs. But the queue past this point looks thin.

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Digital

Discover a new era of healthcare panel engagement: Grounded ...

A new webinar from Konovo will address some of the critical topics impacting today’s healthcare market research industry.

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