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Tuesday 9 June 2026

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News

Vincenzo Nigro, coordinator of the Telethon Undiagnosed Diseases Programme

Italy leads the way on child genetic disease diagnosis

A scheme to hasten the diagnosis of children with genetic disorders is achieving strong results and could be a template for national health systems.

News

FDA clears first gene therapy for rare genetic disease WAS

Fondazione Telethon's Waskyra has become the first gene therapy in the US for Wiskott-Aldrich syndrome, and the first taken to market by a non-profit.

Editor's Picks

Servier wagers $2.65bn on Edgewise muscular dystrophy drug

ASCO26: AZ triplet makes waves in frontline liver cancer

ASCO26: Big win for Erleada in perioperative prostate cancer

Lilly licenses Hanmi GLP-2 drug in $1.26bn deal

First human trial backs AI-designed 'universal' vaccine

Oncology

ASCO 2026: Chinese firms take a front seat in oncology, with...

Dr Li Mao and Dr Giovanni Selvaggi of Betta Pharmaceuticals and Xcovery Holdings discuss their novel ALK inhibitor and the Chinese biotech landscape.

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Digital

Discover a new era of healthcare panel engagement: Grounded ...

A new webinar from Konovo will address some of the critical topics impacting today’s healthcare market research industry.

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