News Clinigen educates on early access to rare disease therapies On Rare Disease Day, Clinigen has launched a campaign to try to encourage doctors and patients to explore how they can get early access to investigational therapies.
Views & Analysis Ensuring access: how to help patients seeking experimental t... The impact of the debate on the Right-to-Try laws in the US and what needs to be done to improve access to innovative drugs.
News Third death reported with a Sarepta gene therapy A third fatality has been recorded among patients receiving treatment with a Sarepta gene therapy, adding to the troubles being faced by the company.
Market Access The value of a partner, globally and locally A new podcast looks at recent trends related to drug approvals, as well as challenges and opportunities both small and large pharma companies face