Duchenne muscular dystrophy

Disease Spotlight

Growing concept eco Group three hand children planting together

Increase collaboration to widen access to DMD drugs, trials ...

When it comes to fighting a rare disease like Duchenne muscular dystrophy (DMD), it’s a matter of strength in numbers.

News

Pfizer axes development of Duchenne muscular dystrophy antib...

Pfizer has axed trials of its domagrozumab antibody for Duchenne muscular dystrophy (DMD), after it failed against efficacy targets.

News

Sarepta dives deeper into gene therapy

Sarepta Therapeutics has handed $30 million to Lacerta in exchange for a group of gene therapies, including a Pompe disease candidate.

Views & Analysis

Parenting as a DMD patient

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He ain’t heavy – learning about a sibling’s DMD diagnosis

It’s common for patients to want to know more about what’s causing them to be ill and their DMD diagnosis and it’s the same for their families – however long that road may be.

Partner Content

Partner Content

An experimental gene therapy for DMD shows positive results

Cell & Gene Therapy 2018