Duchenne muscular dystrophy

News

Pfizer axes development of Duchenne muscular dystrophy antib...

Pfizer has axed trials of its domagrozumab antibody for Duchenne muscular dystrophy (DMD), after it failed against efficacy targets.

News

Sarepta dives deeper into gene therapy

Sarepta Therapeutics has handed $30 million to Lacerta in exchange for a group of gene therapies, including a Pompe disease candidate.

Views & Analysis

Parenting as a DMD patient

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He ain’t heavy – learning about a sibling’s DMD diagnosis

It’s common for patients to want to know more about what’s causing them to be ill and their DMD diagnosis and it’s the same for their families – however long that road may be.

Partner Content

Partner Content

An experimental gene therapy for DMD shows positive results

Cell & Gene Therapy 2018

News

Summit shares plunge nearly 80% after DMD drug fails

Summit Therapeutics has axed development of its Duchenne muscular dystrophy drug ezutromid after a spectacular failure in phase 2, causing the UK biotech's shares to plunge.

Pfizer axes development of Duchenne muscular dystrophy antib...

Sarepta dives deeper into gene therapy

Parenting as a DMD patient

He ain’t heavy – learning about a sibling’s DMD diagnosis

An experimental gene therapy for DMD shows positive results

Summit shares plunge nearly 80% after DMD drug fails

Bayer trial combines two top drugs for kidney disease

Where innovation meets collaboration: Live from Manchester’s...

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Duchenne muscular dystrophy

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