Patients Views & Analysis

Views & Analysis

The urgent need for education and awareness about mitochondr...

Delayed diagnosis, misdiagnosis, and no cure or disease modifying treatments – children living with mitochondrial disease face all the issues often associated with rare diseases.

Views & Analysis

Inclusive research and tackling health inequalities

Health inequalities are a long-term condition and inclusive research is the only disease modifying therapy in the pipeline – but how can the community drive practical change?

Views & Analysis

‘Knowledge is power’ for rare diseases and NAbs

Cure Rare Disease’s Rich Horgan discusses the importance of NAbs screening and helping rare disease patients better understand their level neutralizing antibodies as it relates to gene ther

Views & Analysis

How the community developed fertile ground for progress in rare disease drug development

How the rare disease community has developed fertile ground ...

Amanda Barrell explores how a perfect storm of changing economics, advances in technology, and the increasing volume of the patient voice is stoking change in the rare disease space.

Views & Analysis

COVID-19 lessons for how pharma should support patient advoc...

Trio Health's Neil McGregor-Paterson asks whether the healthcare industry has paid enough attention to the patient voice during COVID-19 and looks at the many ways pharma can improve the patient

Views & Analysis