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A giemsa stained blood smear from a person with beta thalassaemia

First CRISPR drug Casgevy gets swift second approval

The FDA has lost no time in approving Vertex Pharma and CRISPR Therapeutics pioneering gene-editing therapy Casgevy for its second use, approving the drug for transfusion-

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bluebird unveils $2.8m price for gene therapy Zynteglo on FD...

bluebird bio's Zynteglo has become the first cell-based gene therapy to be approved in the US, getting the nod from the FDA as a treatment for patients with beta thalassaemia who require re

News

EMA finds possible link between mRNA COVID jabs and myocardi...

The EU medicines regulator has said that there is some evidence to suggest a possible link between mRNA-based vaccines for COVID-19 and rare cases of heart inflammation.

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engineering and genetic editing through the Crispr technique. DNA chain breaking down. 3D rendering

Zynteglo halt re-ignites viral vector safety concerns; analy...

Bluebird Bio’s decision to hit pause on the launch of Zynteglo for beta thalassaemia after two cases of cancer were seen in a clinical trial could see fears over the safety of viral vectors

News

bluebird bio 'baffled' after NICE rejects beta-thalassaemia ...

It’s back to the drawing board for bluebird bio and its discussions with NICE, which has rejected its beta thalassaemia gene therapy Zynteglo for regular NHS use in first draft guidance.

News

bluebird offers instalment payments for Zynteglo gene therap...

bluebird bio is pricing its thalassaemia gene therapy Zynteglo at €1.57 million ($1.8 million) in Europe, but with an outcomes-based payment scheme to try to persuade healthcare systems to

First CRISPR drug Casgevy gets swift second approval

bluebird unveils $2.8m price for gene therapy Zynteglo on FD...

EMA finds possible link between mRNA COVID jabs and myocardi...

Zynteglo halt re-ignites viral vector safety concerns; analy...

bluebird bio 'baffled' after NICE rejects beta-thalassaemia ...

bluebird offers instalment payments for Zynteglo gene therap...

World Without Disease initiative: 2024 update

The AI effect in pharma commercial strategy: From data to re...

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