Views & Analysis SMA Awareness Month: How pharma and digital solutions can im... Spinal Muscular Atrophy (SMA) is a rare disease affecting the motor nerve cells in the spinal cord.
News Neurogene drops high-dose arm in Rett study after death The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died
Sales & Marketing Coming soon: The Life Sciences Industry Report 2025 – insigh... Prepare for 2025 with pharmaphorum’s Life Sciences Report, featuring expert insights on AI in drug development, gene therapy, and top industry trends
