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5th Oligonucleotides for CNS Summit

The Oligonucleotides for CNS Summit returns for its 5th year to address key challenges in durability, scalability, potency and CNS tropism

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PTC's Huntington study was positive. Why did its stock fall?

In a potentially pivotal trial, PTC Therapeutics' therapy for Huntington's disease met its primary endpoint, but there are questions about the data.

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Woman pushing man in wheelchair along beachfront as sun sets

Novartis pays $1bn upfront for Huntington's drug from PTC

Novartis has made a return to the Huntington's disease stage by licensing an oral mRNA splicer from PTC Therapeutics for $1 billion upfront.

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Boehringer targets NASH/MASH with $2bn Ribo alliance

Boehringer Ingelheim has signed a multi-target collaboration with China’s Suzhou Ribo Life Science and its Swedish unit Ribocure to develop treatments for non-alcoholic or

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RNA Therapy Improves Vision in Child Blindness-More developm...

10th Annual RNA Therapeutics returns to London

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MiNA Therapeutics Chief Scientific Officer to speak at RNA T...

CSO of MiRNA Therapeutics to speak at RNA Therapeutics

5th Oligonucleotides for CNS Summit

PTC's Huntington study was positive. Why did its stock fall?

Novartis pays $1bn upfront for Huntington's drug from PTC

Boehringer targets NASH/MASH with $2bn Ribo alliance

RNA Therapy Improves Vision in Child Blindness-More developm...

MiNA Therapeutics Chief Scientific Officer to speak at RNA T...

NHS "isn't delivering equitable care for rare diseases"

Using AI-driven synthetic personas to take your insights fur...

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