News US and EU regulators collaborate on rare diseases Clinical trial design among areas regulators will collaborate on
News Biomarker trial to show drug value in rare lung disease Growing incidence of IPF raises need for better means of determining diagnosis and treatment success.
News Vertex hit by phase 3 cystic fibrosis failure Company looks to other CF sub-groups to yield success
Views & Analysis Meeting the challenges of rare disease treatment adherence HCPs, pharma and patients can pool their experience to develop effective, tailored support.
News Europe delays review of PTC's Duchenne drug Review of marketing authorisation delayed, new trial likely.
News GBL joins CVC in €10.7bn takeover bid for Recordati A consortium of investors has made a €10.7bn offer to take Italian pharma Recordati private, but some analysts are sceptical the deal will go through.
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