News Charities unite to oppose NICE rare disease rules MPs to discuss controversial plan in special debate.
News FDA fast tracks Shire clotting disease drug The US regulator has given a Fast Track designation to a Shire pipeline drug for a life-threatening blood clotting disease, hereditary thrombotic thrombocytopenic purpura.
Views & Analysis Horses or zebras: inspiring behavioural change to make the r... Insight into human behaviour allows development of programmes that help doctors diagnose rare diseases.
News Thanks Mr President, but you’re wrong about FDA, says rare d... NORD patient advocacy group responds to Congress speech
News Teva files orphan blockbuster hope in tardive dyskinesia SD-809 will be vital for Teva if approved.
Oncology On the benefits of earlier oncological intervention, with Jo... As ESMO 2026 came to a close, pharmaphorum web editor Nicole Raleigh spoke with Johnson & Johnson Innovative Medicine’s Carolyn Sousa and Henar Hevia
Digital Sponsored Discover a new era of healthcare panel engagement: Grounded ... A new webinar from Konovo will address some of the critical topics impacting today’s healthcare market research industry.
