News No safety concerns so far in Sangamo’s groundbreaking gene-e... The trial of Sangamo’s gene-editing treatment for a rare and debilitating disease has got off to a good start, with no safety concerns reported so far.
News New Vertex drugs could help 90% of cystic fibrosis patients Vertex soars after news that tens of thousands of cystic fibrosis (CF) patients could benefit from treatment for the first time.
News EU regulators back Chiesi drug for rare inherited disease Decision paves way for licence to treat alpha-mannosidosis,
News AZ's asthma drug Fasenra approved in EU A further 3,400 children are eligible for treatment with Orkambi
News Pharma collaborates to improve chances of NICE backing Duche... Project will initially focus on DMD but could benefit other rare diseases
News GBL joins CVC in €10.7bn takeover bid for Recordati A consortium of investors has made a €10.7bn offer to take Italian pharma Recordati private, but some analysts are sceptical the deal will go through.
Digital Sponsored Discover a new era of healthcare panel engagement: Grounded ... A new webinar from Konovo will address some of the critical topics impacting today’s healthcare market research industry.