News uniQure presses 'refresh' on haemophilia gene therapy, gets ... Biotech has been in talks with US and EU regulators
Views & Analysis Rare disease market research needs a multifaceted approach Challenges in rare disease market research and the role of online research.
News FDA experts to vote on Spark's groundbreaking gene therapy Luxturna could be single life-changing injection
News Ablynx soars after blood clot trial success European regulators are already reviewing caplacizumab
News PTC Therapeutics fails to convince FDA panel about DMD drug FDA advisers have voted against approval for PTC Therapeutics’ Duchenne drug Translarna because of doubts about its efficacy.
News FDA reviewers slam PTC's Duchenne drug ahead of meeting FDA staff not persuaded by patchy clinical trial evidence for Translarna.
R&D The long-delayed promise of the microbiome, with Sam Possemi... Sam Possemiers, CEO of MRM Health, believes that the microbiome space is finally coming into maturity.
Sales & Marketing Sponsored How to meet your physicians where they are online A pharma company’s core mission is to improve patient outcomes. This hinges on effectively influencing HCP clinical behaviour and driving disease education.