News Vertex's Orkambi CF drug okayed for funding in Australia Committee recommends outcomes-based deal
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Partner Content Partner Content How challenges like Brexit & insufficient patients hinde... Challenges facing Orphan Drugs & Rare Diseases Research
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News Ultragenyx to slash costs after Angelman trial failure Ultragenyx's therapy for the rare genetic disorder Angelman syndrome, apazunersen, has flunked a late-stage trial, crashing its share price.
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