News No safety concerns so far in Sangamo’s groundbreaking gene-e... The trial of Sangamo’s gene-editing treatment for a rare and debilitating disease has got off to a good start, with no safety concerns reported so far.
News New Vertex drugs could help 90% of cystic fibrosis patients Vertex soars after news that tens of thousands of cystic fibrosis (CF) patients could benefit from treatment for the first time.
News EU regulators back Chiesi drug for rare inherited disease Decision paves way for licence to treat alpha-mannosidosis,
News AZ's asthma drug Fasenra approved in EU A further 3,400 children are eligible for treatment with Orkambi
News Pharma collaborates to improve chances of NICE backing Duche... Project will initially focus on DMD but could benefit other rare diseases
News Neuralink unveils trial linking brain implant to robotic arm Neuralink has been given regulatory approval to start a new trial of its brain implant to see if it can be used to control a robotic arm
Sales & Marketing Coming soon: The Life Sciences Industry Report 2025 – insigh... Prepare for 2025 with pharmaphorum’s Life Sciences Report, featuring expert insights on AI in drug development, gene therapy, and top industry trends
