rare disease clinical trials

R&D

Yellow origami boat sailing a different path than a line of white origami boats

Webinar recap: The future of cell and gene therapy in rare d...

For decades, treatment options for rare diseases have been limited, often focusing on symptom management rather than addressing the root cause of them

R&D

On a journey to diverse, inclusive, and more efficient rare ...

Although orphan drugs represent a sizeable portion of new drug approvals,1most rare diseases still lack effective treatment.

News

AI represented of a woman with crow's feet

AbbVie files fast-acting Botox successor in US

AbbVie is hoping to extend its range of neurotoxin-based pharma and cosmetic products with a short-acting successor to its blockbuster Botox brand.

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Sales & Marketing

Health Trends 2025: Reimagining What's Possible

Join the conversation, on Tuesday 28th January @ 10 am ET - 3 pm GMT - 4 pm CET, in our webinar sponsored by Syneos Health, entitled ‘Health Trends 2025: Reimagining What's Possibl

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-Slider in events
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-Spotlight
--Understanding HCPs
--Future of Generics
--Frontiers Health 2022
--Frontiers Health 2021
--Behavioural Science
--ASCO 2019 Live coverage
--AI in Pharma Marketing
--ASCO 2019 and the future of oncology
-Startups
--Views & Analysis
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-System
-Top pharmaceutical companies
--Bristol-Myers Squibb
--Teva
--Roche
--Pfizer
--Novo Nordisk
--Novartis
--Merck Inc
--GlaxoSmithKline
--Gilead
--AstraZeneca
--AbbVie
-Top pharmaceutical companies
--Merck Inc
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--Brexit
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--M&A
-Top stories
-About pharmaphorum
-Top pharmaceutical companies
--Gilead
--Merck Inc
--Teva
--Roche
--Pfizer
--Novo Nordisk
--Novartis
--GlaxoSmithKline
--Bristol-Myers Squibb
--AstraZeneca
--AbbVie
-test webinar
-System
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-barelonalive 2016
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-ASCO 2019 and the future of oncology
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-Behavioural Science
-Frontiers Health 2021
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-Future of Generics
-Life Sciences Industry Report
-Understanding HCPs
-World Without Disease Summit
-The Future of Generics

rare disease clinical trials

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