Orphan Drugs & Rare Diseases

Digital

To fight rare diseases, win the data battle first

Innovation is the key to evolution. In the pharmaceutical space, brilliant advancements have occurred with drugs with large population pools.

Partner Content

Partner Content

Invitation to SMI’s Orphan Drugs & Rare Diseases Conference ...

SMi reports: Invitation from conference co-chair released for the 9th Annual Orphan Drugs & Rare Diseases conference, taking place in London this October

Oncology

Interview at ASCO 2025 with Dr Danny Nguyen

In pursuit of a cure for cancer: An ASCO 2025 discussion wit...

Dr Danny Nguyen, medical oncologist and haematologist at the City of Hope Orange County, spoke with pharmaphorum at ASCO 2025.

Market Access

pharmaphorum podcast Episode 178a - Sandra Anderson and Chris Williams, Cencora

The value of a partner, globally and locally

A new podcast looks at recent trends related to drug approvals, as well as challenges and opportunities both small and large pharma companies face

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--Frontiers Health 2022
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--ASCO 2019 and the future of oncology
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--Bristol-Myers Squibb
--Teva
--Roche
--Pfizer
--Novo Nordisk
--Novartis
--Merck Inc
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--Gilead
--AstraZeneca
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Orphan Drugs &amp; Rare Diseases

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Orphan Drugs & Rare Diseases