Views & Analysis
![Balancing-expectations](https://pharmaphorum.com/wp-content/uploads/2018/10/Balancing-expectations-16x9.jpg)
Balancing expectations: An unmet need in the orphan disease ...
There are between 6000 and 8000 rare diseases in the world, and one in ten people in Europe and the US have a rare disease; 75% of rare diseases affect children, and 30% of rare disease patients di