gene editing

News

After a no in sickle cell, NICE OKs Casgevy for thalassaemia

Vertex and CRISPR Therapeutics have won the backing of NICE for their gene-editing therapy Casgevy as a treatment for the blood disorder beta thalassaemia, a few months after turning it dow

News

Vertex, Orum partner on safer pre-treatment for gene meds

Vertex Pharma has teamed up with Orum Therapeutics to develop a conditioning regimen, used to prepare patients to receive gene-editing medicines, that it hopes will offer a more tolerable a

Digital

Working for a mature form of genomic medicines

In a new episode of the pharmaphorum podcast, Rahul Kakkar, CEO of gene editing company Tome, speaks with web editor Nicole Raleigh about programmable genomic integration (PGI) technology.<

News

Prime editing comes of age as FDA clears human trials

Prime Medicine has been given the go-ahead by the FDA for the first human trial of its prime editing technology, which promises to deliver one-shot therapies for a range o

R&D

Partner Content

3rd In Vivo Cell Engineering & Gene Editing Summit

Achieve Safe & Targeted In Vivo Delivery of Payloads with Clarity in Regulations & Appropriate Models to Advance the Next Frontier of In Vivo Editing from Research to Clinic

News

Dr Andrew Anzalone, Prime Medicine co-founder and head of platform development

Gene-editing firm Prime Medicine files $140m public offer

Gene-editing biotech Prime Medicine has priced a follow-on public offering, hoping to raise $140 million to advance its pipeline of one-shot therapies for severe genetic d

After a no in sickle cell, NICE OKs Casgevy for thalassaemia

Vertex, Orum partner on safer pre-treatment for gene meds

Working for a mature form of genomic medicines

Prime editing comes of age as FDA clears human trials

3rd In Vivo Cell Engineering & Gene Editing Summit

Gene-editing firm Prime Medicine files $140m public offer

Unpacking Trump’s executive order on drug pricing, with Alic...

Health Trends 2025: Reimagining What's Possible

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