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FDA grants fast review for Horizon’s rare eye disease drug
https://pharmaphorum.com/news/fda-grants-fast-review-for-horizons-rare-eye-disease-drug/
eye disease
NICE rejects rare eye disease therapy
Other treatment option is disfiguring eyelid operation
Living with LHON: Achieving your dreams in the dark
When Fabrizio Sottile went blind at the age of 17, he thought his dreams of becoming a world-class swimmer were over. But he wasn’t about to let Leber’s hereditary optic neuropathy (LHON) stand in his way, and he made his first appearance as part of Italy’s Paralympic team in 2016, aged 23.
Out of the darkness: new gene therapies for eye diseases
US FDA expert committee’s ‘yes’ could pave the way for a new generation of gene therapies for rare inherited eye disorders.