Cambridge Rare Disease Network Archives -

To help pharma companies understand what life is really like for patients with a rare disease, a new

Rare disease insights from the patient community

https://pharmaphorum.com/views-and-analysis/rare-disease-insights-from-the-patient-community/

Delayed diagnosis, lack of awareness, and a limited evidence base – Aarskog syndrome faces all the challenges of

Flying the flag for research in Aarskog syndrome

https://pharmaphorum.com/views-analysis-patients/flying-the-flag-for-research-in-aarskog-syndrome/

As Rare Disease day 2020 approaches, we take a look at the biggest challenges facing orphan drug developers

The biggest challenges facing rare disease pharma – and how the industry can tackle them

https://pharmaphorum.com/r-d/views-analysis-r-d/biggest-challenges-rare-disease/

A family tragedy has prompted Kay Parkinson, founder of the rare disease charity Alstrom Syndrome UK, to create

Raising awareness about rare diseases

https://pharmaphorum.com/views-analysis-patients/awareness-rare-diseases/

The lessons that can be learned for the future of drug development from the collaboration and innovation in this space.

Tunnah’s musings: Rare diseases hold key to future of drug development

https://pharmaphorum.com/views-and-analysis/tunnahs-musings-rare-diseases-hold-key-future-drug-development/

Cambridge Rare Disease Network