BioMarin Archives -

FDA slaps clinical hold on BioMarin’s PKU gene therapy

https://pharmaphorum.com/news/fda-slaps-clinical-hold-on-biomarins-pku-gene-therapy/

2nd Gene Therapy for Blood Disorders

https://pharmaphorum.com/events/2nd-gene-therapy-for-blood-disorders/

BioMarin files achondroplasia drug after rejection for haemophilia therapy

https://pharmaphorum.com/news/biomarin-files-achondroplasia-drug-after-rejection-for-haemophilia-therapy/

Girl loses High Court battle over NICE review of BioMarin’s PKU drug

https://pharmaphorum.com/news/girl-loses-high-court-battle-over-nice-review-of-biomarins-pku-drug/

Child with rare disease takes NICE to court over access to life-changing therapy

https://pharmaphorum.com/news/child-with-rare-disease-takes-nice-to-court-over-access-to-life-changing-therapy/

BioMarin seeks haemophilia gene therapy approval after promising data

https://pharmaphorum.com/news/biomarin-seeks-haemophilia-gene-therapy-approval-after-promising-data/

Final NICE rejection for Biomarin’s childhood rare disease drug

https://pharmaphorum.com/news/final-nice-rejection-for-biomarins-childhood-rare-disease-drug/

Gene therapy firm BioMarin stages haemophilia musical

https://pharmaphorum.com/news/gene-therapy-firm-biomarin-stages-haemophilia-musical/

FDA approves new treatment for rare genetic disease PKU

https://pharmaphorum.com/news/fda-approves-new-treatment-for-rare-genetic-disease-pku/

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