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Evidence builds behind Regeneron's deafness gene therapy

Ten out of 11 children with congenital deafness treated with a gene therapy developed by Regeneron have seen "notable" improvements in hearing.

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Ex-CDER chief Cavazzoni rejoins Pfizer as CMO

In a move that will raise eyebrows in Washington, Pfizer has hired former FDA director Patricia Cavazzoni as its new chief medical officer.

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Troubled gene therapy player bluebird sold for a song

At risk of defaulting on financial commitments, gene therapy firm bluebird bio has agreed to sell itself to private equity firms at a knockdown price.

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Trial of Boehringer's cystic fibrosis gene therapy imminent

Boehringer's cystic fibrosis gene therapy is poised to start clinical testing, hoping to offer a one-shot alternative to costly CFTR modulator drugs.

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Poolbeg slumps as Hookipa merger is called off

A proposed merger of the UK's Poolbeg with Austrian biotech Hookipa has been called off after the latter abruptly withdrew from negotiations.

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SMA treatment with Evrysdi 'could start prenatally'

Should treatment of neurodegenerative disorder SMA with Roche's Evrysdi start even before birth? One case study suggests so.

Evidence builds behind Regeneron's deafness gene therapy

Ex-CDER chief Cavazzoni rejoins Pfizer as CMO

Troubled gene therapy player bluebird sold for a song

Trial of Boehringer's cystic fibrosis gene therapy imminent

Poolbeg slumps as Hookipa merger is called off

SMA treatment with Evrysdi 'could start prenatally'

Merck rare tumour drug Ezmekly backed for NHS use

Discover a new era of healthcare panel engagement: Grounded ...

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