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FDA clears first gene therapy for rare genetic disease WAS

Fondazione Telethon's Waskyra has become the first gene therapy in the US for Wiskott-Aldrich syndrome, and the first taken to market by a non-profit.

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UK confirms lower clawback rate for NHS medicines

The UK has cut its voluntary rebate rate for new medicines supplied to the NHS to 14.5% next year, but industry says this is "only the first step."

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CDC panel votes to scrap hepatitis B birth dose advice

CDC advisers vote to overturn decades of US policy and abandon endorsement of universal hepatitis B vaccination for newborns in the US.

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NHS use of digital cardiac rehab tools endorsed

Seven digital health technologies used to support people recovering from cardiovascular diseases have been recommended for use by the NHS.

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Pazdur to leave FDA, shortly after taking CDER job

Long-serving FDA figure Richard Pazdur has filed papers to retire, shortly after being appointed to lead CDER, according to reports.

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Bayer aims Mirena at women's health issue with no treatment

Bayer has started a phase 3 trial of its Mirena contraceptive in an endometrial disorder, with no treatments, that can lead to cancer.

FDA clears first gene therapy for rare genetic disease WAS

UK confirms lower clawback rate for NHS medicines

CDC panel votes to scrap hepatitis B birth dose advice

NHS use of digital cardiac rehab tools endorsed

Pazdur to leave FDA, shortly after taking CDER job

Bayer aims Mirena at women's health issue with no treatment

Lilly bags FDA okay for Wegovy pill rival orforglipron

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