News Wave surges on first RNA editing data in humans Shares in Wave Life Sciences rose by 74% after it reported clinical data with a pioneering new RNA-editing therapy for alpha-1 antitrypsin deficiency (AATD).
R&D Partner Content 5th RNA Editing Summit 2024 Pioneering RNA Editing Drugs Towards Clinical Realities
News Neurogene drops high-dose arm in Rett study after death The patient affected by a serious adverse event in Neurogene's clinical trial of Rett syndrome gene therapy has now died
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