Views & Analysis LHON in the family: living under the spectre of an hereditar... It’s hard to imagine suddenly losing your sight in your 20s, but that’s what happened to Richard Wheeler when he developed
Views & Analysis Out of the darkness: new gene therapies for eye diseases US FDA expert committee’s ‘yes’ could pave the way for a new generation of gene therapies for rare inherited eye disorders.
Views & Analysis Getting a rarer perspective Benefitting from insights from focus groups with rare disease patients.
R&D The long-delayed promise of the microbiome, with Sam Possemi... Sam Possemiers, CEO of MRM Health, believes that the microbiome space is finally coming into maturity.
Sales & Marketing Sponsored How to meet your physicians where they are online A pharma company’s core mission is to improve patient outcomes. This hinges on effectively influencing HCP clinical behaviour and driving disease education.