Views & Analysis LHON in the family: living under the spectre of an hereditar... It’s hard to imagine suddenly losing your sight in your 20s, but that’s what happened to Richard Wheeler when he developed
Views & Analysis Out of the darkness: new gene therapies for eye diseases US FDA expert committee’s ‘yes’ could pave the way for a new generation of gene therapies for rare inherited eye disorders.
Views & Analysis Getting a rarer perspective Benefitting from insights from focus groups with rare disease patients.
News Regeneron swoops on genetic testing firm 23andMe DNA testing company 23andMe looks destined to be taken over by a pharma company, as Regeneron agrees a $256 million acquisition deal.
Market Access Sponsored Bridging research and clinical guidelines – interactive stra... Medical affairs is evolving. Understanding how to harness real-world data and digital insights is essential.