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Science Molecule, Molecular DNA Model Structure, business teamwork conceptMolecular, DNA and atom model in science research labMolecular, DNA and atom model in science research lab setting in studio.

Duchenne drug available in England within weeks after NICE a...

PTC Therapeutics’ Translarna (ataluren) will be available to Duchenne muscular dystrophy patients “within weeks”, NICE has said, after a deal was agreed with the manufacturer.

News

Vertex Pharmaceutical's Boston headquarters

FDA clears two sickle-cell gene therapies, including CRISPR ...

The US FDA announced today that it has cleared two novel gene therapies for sickle cell disease: Vertex Pharmaceuticals' Casgevy and bluebird bio's Lyfgenia.

R&D

Revolutionising research: Inside the NCVR evolution in the U...

On 1st October, the roll-out of the National Contract Value Review (NCVR) process marked a pivotal moment in the trajectory of clinical research in the UK, introducing a standardised, natio

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