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NICE rejects Orchard’s gene therapy for rare childhood disease MLD
https://pharmaphorum.com/news/nice-rejects-orchards-gene-therapy-for-rare-childhood-disease-mld/
Orchard Therapeutics
Orchard raises $150m to develop gene therapies
Biotech has trio of rare disease therapies
Orchard’s gene therapy gains UK ‘promising innovative medicine’ status
A UK biotech start-up has gained a sought after ‘promising innovative medicine’ (PIM) designation for its ultra-rare disease gene therapy.