NHS signs deal with Orchard for pricey Libmeldy gene therapy
gene therapy, HEOR, Libmeldy, NHS, NICE, Orchard Therapeutics, paediatric, rare disease
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Orchard Therapeutics
NICE rejects Orchard’s gene therapy for rare childhood disease MLD
gene therapy, HEOR, Libmeldy, NICE, Orchard Therapeutics, paediatric, rare disease
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Orchard raises $150m to develop gene therapies
gene therapy, GlaxoSmithKline, Orchard Therapeutics
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Biotech has trio of rare disease therapies
Orchard’s gene therapy gains UK ‘promising innovative medicine’ status
gene therapy, MHRA, Orchard Therapeutics, Promising Innovative Medicine, Rare diseases, ultra-rare diseases
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A UK biotech start-up has gained a sought after ‘promising innovative medicine’ (PIM) designation for its ultra-rare disease gene therapy.