metachromatic leukodystrophy

News

Spain agrees to reimburse Orchard's gene therapy Libmeldy

Spain has agreed to reimburse Orchard Therapeutics' ex vivo gene therapy for the rare childhood disease metachromatic leukodystrophy.

News

Orchard’s MLD gene therapy becomes costliest US medicine

Orchard Therapeutics has revealed its US pricing plans for Lenmeldy, its gene therapy for metachromatic leukodystrophy (MLD), placing a $4.25 million price tag on the one-

News

Orchard's gene therapy for MLD finally gets US approval

The FDA has cleared its first gene therapy for kids with metachromatic leukodystrophy (MLD), a rare genetic disorder of the brain and nervous centre.

Spain agrees to reimburse Orchard's gene therapy Libmeldy

Orchard’s MLD gene therapy becomes costliest US medicine

Orchard's gene therapy for MLD finally gets US approval

NHS "isn't delivering equitable care for rare diseases"

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metachromatic leukodystrophy

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