gene therapy

News

Second death in gene therapy trial prompts investigation

A second death in a study of Novartis’ spinal muscular atrophy gene therapy Zolgensma (onasemnogene abeparvovec-xioi; AVXS-101) – a potential blockbuster for this rare disease – has prompte

News

Catalent acquires gene therapy specialist Paragon for $1.2bn

Drug delivery technology provider Catalent is to acquire gene therapy company Paragon for $1.2 billion.

News

Roche insists Spark deal is still on, despite lacklustre tak...

Shareholders in Spark Therapeutics haven’t been queueing up to take advantage of Roche’s $114.50-per-share offer, forcing an extension to the tender process.

News

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UK health innovations get £23m funding

The UK government’s Biomedical Catalyst (BMC) programme has announced £23 million of funding for cutting edge health projects, including new software which enables radiologists to diagnose

Views & Analysis

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Gene addition – a new chapter in treating rare diseases

The scientific advancements of the past 30 years have transformed our understanding of the potential of gene therapy and how it may be used to tackle rare diseases.

R&D

Will cell and gene therapies disrupt reimbursement?

Cell and gene therapies could prove disruptive in terms of the life-changing benefits they could bring to people with rare diseases and cancers – but they could also mean healthcare systems

Second death in gene therapy trial prompts investigation

Catalent acquires gene therapy specialist Paragon for $1.2bn

Roche insists Spark deal is still on, despite lacklustre tak...

UK health innovations get £23m funding

Gene addition – a new chapter in treating rare diseases

Will cell and gene therapies disrupt reimbursement?

CDC panel votes to scrap hepatitis B birth dose advice

How to meet your physicians where they are online

gene therapy

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