Charcot-Marie-Tooth

News

Augustine decloaks with $85m for nerve disease programme

Belgian start-up Augustine raises €78m ($85m) in first-round funding for HDAC6 inhibitors headed by a candidate for Charcot-Marie-Tooth disease.

News

Pharnext hit again as rare disease drug flunks phase 3 test

French biotech Pharnext has seen the value of its shares collapse after it revealed that its lead drug, a treatment for Charcot-Marie-Tooth (CMT) disease, failed to make t

R&D

Jonah Comstock interviews Dr Dhaval Shah at AAPS

Modelling biologics: Challenges and opportunities, with Dr D...

From AAPS 2025, an interview with Dr Dhaval Shah, professor of pharmaceutical sciences at the University of Buffalo and former Pfizer researcher.

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Market Access

Bridging research and clinical guidelines – interactive stra...

Medical affairs is evolving. Understanding how to harness real-world data and digital insights is essential.

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