adrenoleukodystrophy

News

Refiling for cALD therapy on the cards after new data

Readout from NEXUS study sets up mid-2025 refiling for Minoryx and Neuraxpharm's leriglitazone for rare disease cerebral adrenoleukodystrophy (cALD).

News

New film aims to raise awareness of rare disease cALD

Rare Disease Day saw the debut of a film that aims to raise awareness of cerebral adrenoleukodystrophy (cALD), a devastating and fatal condition with no pharmacological tr

News

How-cell-and-gene-therapies-are-transforming-the-pace-of-deal-making

SwanBio raises $56m for rare neurological disease gene thera...

SwanBio Therapeutics has raised $56 million in a second-round financing that will be used to advance its lead gene therapy candidate for adrenomyeloneuropathy (AMN) into clinical testing la

Refiling for cALD therapy on the cards after new data

New film aims to raise awareness of rare disease cALD

SwanBio raises $56m for rare neurological disease gene thera...

Direct-to-patient is more than just telehealth – with EVERSA...

Health Trends 2025: Reimagining What's Possible

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