Fresh thinking and greater collaboration at the European level could accelerate the much-needed development of treatments and cures for children with rare diseases.
While the industry appears united in its commitment to patient centricity, the practicalities of embedding the ethos into everyday work is still hotly debated.
GP Karishma Patel tells us about the daily challenges of living with the ultra-rare condition Familial Chylomicronaemia Syndrome (FCS), which prevents the body from breaking down fats.
eyeforpharma's Patient Summit Europe brought together leading patient innovators from industry and patient associations for two days of sharing, learning and a healthy dose
A pharma company’s core mission is to improve patient outcomes. This hinges on effectively influencing HCP clinical behaviour and driving disease education.