PTC Therapeutics

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PTC's Huntington study was positive. Why did its stock fall?

In a potentially pivotal trial, PTC Therapeutics' therapy for Huntington's disease met its primary endpoint, but there are questions about the data.

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Dyvyzat box, bottle, and oral delivery mechanism.

Italfarmaco closes on EU okay for Duchenne drug

Italfarmaco's oral HDAC inhibitor Duvyzat has been recommended for approval in the EU as a treatment for Duchenne muscular dystrophy (DMD).

News

Woman pushing man in wheelchair along beachfront as sun sets

Novartis pays $1bn upfront for Huntington's drug from PTC

Novartis has made a return to the Huntington's disease stage by licensing an oral mRNA splicer from PTC Therapeutics for $1 billion upfront.

News

PTC gets FDA okay for first brain-delivered gene therapy

More than two years after its approval in Europe, PTC Therapeutics' gene therapy for rare genetic disorder AADC deficiency will soon be made available to patients in the US.

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EU rules PTC’s Duchenne drug can stay on the market

Going against the advice of its own advisors, the European Commission has said that PTC Therapeutics’ Translarna therapy for Duchenne muscular dystrophy (DMD) should stay

News

uniQure craters on Huntington’s gene therapy data

uniQure has presented new results from its phase 1/2 study of its gene therapy for Huntington’s disease that

PTC's Huntington study was positive. Why did its stock fall?

Italfarmaco closes on EU okay for Duchenne drug

Novartis pays $1bn upfront for Huntington's drug from PTC

PTC gets FDA okay for first brain-delivered gene therapy

EU rules PTC’s Duchenne drug can stay on the market

uniQure craters on Huntington’s gene therapy data

Treating primary bone cancer: The potential of listeria-base...

The value of a partner, globally and locally

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PTC Therapeutics

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