PTC Therapeutics

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PTC slides on failed Friedreich ataxia study

PTC Therapeutics has cued up no fewer than three clinical trial readouts this quarter that could lead to new regulatory filings – but the latest for vatiquinone in inherit

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PTC eyes filings for PKU therapy after phase 3 win

PTC Therapeutics is on track to file for approval of a new therapy for rare disease phenylketonuria after a positive phase 3 readout that could extend its product portfoli

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PTC’s gene therapy for rare disease cleared for NHS use

Upstaza has shown impressive clinical results in children with fatal disorder AADC deficiency.

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NICE okays neoadjuvant Opdivo in lung cancer

BMS' checkpoint inhibitor is first to be given a green light for use before surgery in NSCLC.

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Roche puts pressure on SMA rivals with new FDA approval

Roche and PTC Therapeutics' Evrysdi for spinal muscular atrophy (SMA) has been approved by the FDA for younger children with the rare disease, extending its use to include infants less than

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Genetic engineeering concept with 3d rendering robotic hand editing dna helix

PTC gets green light for gene therapy Upstaza in EU

PTC Therapeutic's Upstaza gene therapy for patients with genetic disorder AADC deficiency has been recommended for approval in the EU, setting up another test of the commercial prospects f

PTC slides on failed Friedreich ataxia study

PTC eyes filings for PKU therapy after phase 3 win

PTC’s gene therapy for rare disease cleared for NHS use

NICE okays neoadjuvant Opdivo in lung cancer

Roche puts pressure on SMA rivals with new FDA approval

PTC gets green light for gene therapy Upstaza in EU

Regeneron swoops on genetic testing firm 23andMe

Bridging research and clinical guidelines – interactive stra...

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PTC Therapeutics

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