orphan disease Archives -

New analysis from GlobalData has identified the predicted top 15 pharma players in 2025 for organ drugs, with

Who will be the biggest pharma players in orphan drugs?

https://pharmaphorum.com/views-analysis-sales-marketing/who-will-be-the-biggest-pharma-players-in-orphan-drugs/

There are between 6000 and 8000 rare diseases in the world, and one in ten people in Europe

Balancing expectations: An unmet need in the orphan disease arena

https://pharmaphorum.com/views-analysis-market-access/balancing-expectations-rare-disease-arena/

SMi Reports: AI HealthTech Company Healx, who raised $10m to advance drug discovery and treatments for rare diseases,

Hear from HealthTech Healx which raised $10m to accelerate drug discovery

https://pharmaphorum.com/r-d/partner-content-r-d/healthtech-healx-raise-10m-to-accelerate-drug-discovery/

First treatment approved for Huntington’s Disease in almost a decade.

FDA approves Teva’s Huntington’s Disease drug

https://pharmaphorum.com/news/fda-approves-tevas-huntingtons-disease-drug/

With the appraisal process for highly specialised treatments in the UK described by one NHS insider as ‘impenetrable’,

Funding rare disease treatments in the UK – navigating the labyrinth

https://pharmaphorum.com/views-and-analysis/funding-rare-disease-treatments-in-the-uk-navigating-the-labyrinth/

orphan disease