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Gilead rescinds orphan status request for COVID-19 drug

Gilead has rescinded its request for orphan status for its potential COVID-19 antiviral remdesivir amid a furore over its pricing should it get to market.

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Shire plans filing for HAE drug after phase 3 success

Shire plans to file its lanadelumab for the rare genetic disorder, hereditary angioedema (HAE), on the back of new phase 3 data showing the drug reduces monthly swelling attacks when taken

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Scott Gottlieb confirmed as FDA commissioner

Scott Gottlieb has been confirmed as the next FDA commissioner after Senators voted in favour of president Donald Trump’s pick to run the world’s most influential regulator.

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European union flag against parliament in Brussels, Belgium

EUSA Pharma approval fills gap in neuroblastoma market

EUSA Pharma’s dinutuximab beta has gained European approval for its immunotherapy for children affected by a rare and devastating form of cancer, a move which exploits a gap in the market l

News

EU regulators back two more orphan drugs, question of pricin...

Two orphan medicines are heading towards the European market, after regulators recommended rare disease drugs from Biogen and BioMarin.

News

Novartis and Allergan to combine drugs in NASH

Novartis has joined with Allergan in a bid to get ahead in the race to get a drug approved to treat the fatty liver disease, non-alcoholic steatohepatitis (NASH).

Gilead rescinds orphan status request for COVID-19 drug

Shire plans filing for HAE drug after phase 3 success

Scott Gottlieb confirmed as FDA commissioner

EUSA Pharma approval fills gap in neuroblastoma market

EU regulators back two more orphan drugs, question of pricin...

Novartis and Allergan to combine drugs in NASH

FDA clears two sickle-cell gene therapies, including CRISPR ...

Revolutionising research: Inside the NCVR evolution in the U...

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